Research and Training Programs

In 2020, the SPRING research team completed a multicenter phase III randomized controlled trial fo

The primary objective is to implement a personalized approach to curative therapies for children and adults with sickle cell disease (SCD) to maximize benefits while minimizing adverse outcomes. Current efforts to understand long-term health outcomes after these therapies are limited. The focus on initial treatment success recalls developments in pediatric oncology during the 1980s, where effective therapies eventually led to increased risks of organ dysfunction and malignancies.